Published on Jul 23, 2019
CCMT assistant professor Dr. Ophir Shalem has been selected as a 2019 NIH Director's New Innovator Award recipient. Read more about the award here and the NIH's High-Risk, High-Reward Research program here.
Published on Apr 12, 2017
Congrats to Dr. Beverly Davidson, Raymond G. Perelman CCMT director, on her election to the American Academy of Arts and Sciences! Read more about this prestigious award here.
Published on Apr 26, 2016
Philanthropist gifts $50M to Children's Hospital of Philadelphia for Pediatric Research Campus
The extraordinary endowment will eventually establish the Raymond G. Perelman Campus at CHOP; it will be an 8-acre addition to the hospital.
Published on Feb 1, 2016
The Huntington's Disease (HD) Center founded and directed by the CCMT's own Dr. Pedro Gonzalez-Alegre has been designated a Center of Excellence by the Huntington's Disease Society of America (HDSA) for 2016. Check out our Clinical Programs page for more information on this exciting achievement!
Published on Jan 27, 2016
CHOP treats blood disorder with gene therapy in dogs
Researchers at Children's Hospital of Philadelphia report that they have corrected a rare blood disorder in dogs by administering a single injection of gene therapy.
Published on Jan 21, 2016
Gene Therapy for Rare Bleeding Disorder Achieves Proof-of-Concept
CHOP Researcher Leads Study of Factor VII Deficiency in Dog Model; Shows Long-term Correction, Safety and Feasibility
Published on Nov 13, 2015
Gene Therapy For Batten Disease?
Published on Nov 11, 2015
Batten disease may benefit from gene therapy
Animal study suggests one-shot approach to injecting genes
Published on Nov 11, 2015
Batten disease may benefit from gene therapy
NIH-funded animal study suggests one-shot approach to injecting genes
Published on Nov 11, 2015
Gene Therapy Makes Advances against a Lethal Childhood Disorder
CHOP researchers have taken a significant step forward in developing gene therapy against Batten disease, a fatal neurodegenerative disorder that strikes children