Current Seminars

The Center, in collaboration with Gene Therapy and Vaccines program at the University of Pennsylvania, hosts a seminar series during the academic year with presentations focusing on research progress in therapies for genetic diseases given by national and international speakers. For details, please contact our Center Coordinator at This email address is being protected from spambots. You need JavaScript enabled to view it. or (215) 590-4521.


January 7, 2013
3:00pm-4:00pm Brian K. Kaspar, Ph.D.
Associate Professor, Center for Gene Therapy
The Research Institute at Nationwide Children's Hospital, Cincinnati, OH
"Basic and Translational Studies for Motor Neuron Disease:Spinal Muscular Atrophy and Amyotrophic Lateral Sclerosis"
February 4, 2013
4:00pm-5:00pm Andrew Geall, Ph.D.
RNA Vaccine Platform Leader
Novartis Vaccines & Diagnostics, Inc.
"Non-viral-delivery of self-amplifying RNA vaccines"
March 18, 2013
4:00pm-5:00pm Roland W. Herzog, Ph.D.
Professor of Pediatrics
University of Florida, Gainesville
"Avoiding Immune Rejection of Gene Therapy for Hemophilia"
April 1, 2013
4:00pm-5:00pm Edward Tuddenham, M.D.
Emeritus Professor of Haemophilia
University College London, UK
"In Pursuit of the Eighth Factor--A 40 Year Project"
April 15, 2013
4:00pm-5:00pm Michael C. Milone, M.D., Ph.D.
Assistant Professor of Pathology and Laboratory Medicine
Perelman School of Medicine of the University of Pennsylvania, Philadelphia, PA
"Building Supernatural T Cells for Cancer Therapy"
June 17, 2013
4:00pm-5:00pm Charles Venditti, M.D., Ph.D.
Investigator, National Human Genome Research Institute
National Institutes of Health, Bethesda, MD
"Gene Therapy for Methylmalonic Acidemia: Lessons from Patients and Mice"
September 20, 2013
12:00pm-1:00pm Beverly L. Davidson, Ph.D.
Roy J. Carver Biomedical Research Chair
Roy J. and Lucille A. Carver College of Medicine, University of Iowa, Iowa City, IA
"Advancing Molecular Therapies for Inherited Brian Disease"
123C ARC
October 21, 2013
4:00pm-5:00pm J. Keith Joung, M.D., Ph.D.
Associate Professor of Pathology
Harvard Medical School, Boston, MA
"Genome and Epigenome Editing Using Engineered TALE and CRISPR Technologies"
November 18, 2013
4:15pm-5:15pm Stephan Grupp, M.D., Ph.D.
Professor of Pediatrics
Perelman School of Medicine of the University of Pennsylvania, Philadelphia, PA
December 16, 2013
4:00pm-5:00pm Lishan Su, Ph.D.
Professor of Microbiology & Immunology
University of North Carolina at Chapel Hill, Chapel Hill, NC
"The Good, The Bad, and The Ugly: Immune Effectors in Human Chronic Virus Infection and Therapy"
Co-Sponsored by the University of Pennsylvania Center for AIDS Research


February 6, 2012
4:00pm-5:00pm Brian Brown, Ph.D
Assistant Professor of Genetics
The Mount Sinai Medical Center
“Uncovering the Dynamic Relationship between MicroRNA and Target"
123C ARC
February 20, 2012
4:00pm-5:00pmGeorgia D. Tomaras, Ph.D.
Assistant Professor of Immunology Molecular Genetics and Microbiology
Human Vaccine Institute, Duke University of Medicine
“HIV-1 Envelope IgA Antibodies in Vaccination and Infection"
Co-sponsored by the University of Pennsylvania Center for AIDS Research123C ARC
March 5, 2012
4:00pm-5:00pmLeslie S. Kean, M.D.,Ph.D.
Assistant Professor, Aflac Cancer Center and Blood Disorders Service
Department of Pediatrics and The Emory Transplant Center
Department of Surgery
Director, Children's Transplant Immunology and Immune Therapeutics Center
Emory University School of Medicine
“Insights into Immune Tolerance from Non-Human Primate Models: From T Cells, to Transplants, to Clinical Trials”
123C ARC
March 19, 2012
123C ARC
*April 16, 2012
4:00pm-5:00pmLawrence Corey, M.D.
President and Director, Fred Hutchinson Cancer Research Center
Professor of Medicine and Laboratory Medicine, University of Washington
“Control of HSV Infection: The Action is in the Mucosa”
Co-sponsored by the University of Pennsylvania Center for AIDS Research; *Note special locationClass of '62 Auditorium, John Morgan Building
*May 10, 2012
4:00pm-5:00pmAndrew Davidoff, M.D.
Chair, Department of Surgery
St. Jude Children's Research Hospital
“AAV-Mediated Gene Therapy for Hemophilia B: Bench to Bedside”
*Note special date and location1100B CTRB
May 21, 2012
4:00pm-5:00pmStephanie Cherqui, Ph.D.
Assistant Professor of Molecular and Experimental Medicine
The Scripps Research Institute
“Stem Cell and Gene Therapy-Based Strategies for the Lysosomal Storage Disorder Cystinosis”
123C ARC
June 4, 2012
4:00pm-5:00pmKatherine Parker Ponder, M.D.
Professor of Medicine
Washington University in St. Louis
“A Decade of Gene Therapy for Mucopolysaccharidosis”
123C ARC
June 18, 2012
October 1, 2012
4:00pm-5:00pmJoe N. Kornegay, D.V.M., Ph.D.
Professor of Pathology and Laboratory Medicine
University of North Carolina at Chapel Hill
“Translational Lessons Learned from a Canine Model of Duchenne Muscular Dystrophy”
123C ARC
October 15, 2012
4:00pm-5:00pmMalcolm Brenner, M.D., Ph.D.
Professor of Pediatrics
Baylor College of Medicine
“Moving CARS Forward”
123C ARC

November 5, 2012
4:00pm-5:00pmGuido Ferrari, M.D.
Assistant Professor of Experimental Surgery
Duke Medical Center
123C ARC

*November 15, 2012
4:00pm-5:00pmDwight Koeberl, M.D., Ph.D.
Associate Professor of Pediatrics
Duke Medical Center
*Note special date and location1100A CTRB
December 3, 2012
4:00pm-5:00pmJose R. Conejo-Garcia, M.D., Ph.D.
Associate Professor, Immunology Program
The Wistar Institute
123C ARC
December 17, 2012
4:00pm-5:00pmMargaret G. McGlynn, M.B.A.
President & CEO
International AIDS Vaccine Initiative (IAVI)
123C ARC


January 31, 2011
Antonia Follenzi, M.D.
Assistant Professor of Histology
University of Piemonte Orientale Medical School
" Extrahepatic Cells Produce DVIII and Cure Hemophilia A "
1100A CTRB
February 21, 2011
Robert B. Wilson, M.D., Ph.D.
Professor of Pathology & Laboratory Medicine
University of PA School of Medicine
" Random shRNA Selection "
1100B CTRB
February 23, 2011
Ronald G. Crystal, M.D.
Professor and Chair of Genetic Medicine
Weill Medical College of Cornell University
“Gene Therapy for CNS Disorder "
Co-Sponsored by the University of Pennsylvania Immunology Colloquium
Fisher Translational Research Building Auditorium
May 2, 2011
David W. Scott, Ph.D.
Professor of Medicine & Vice Chair, Research
University Services University of Health Sciences
“Immunization, Deimmunization and Tolerance to Factor VIII "
1100B CTRB
August 10, 2011
Eirini P. Papapetrou, M.D., Ph.D.
Research Associate, Center for Cell Engineering, Molecular Pharmacology and Chemistry Program
Memorial Sloan Kettering Cancer Center
“ Modeling Hematology Disease and Cell Therapy using Induced Pluripotent Stem Cells”
123C ARC
October 13, 2011
Mark A. Kay, M.D., Ph.D.
Dennis Farrey Family Professor, Department of Pediatrics and Genetics, Vice Chair for Basic Research (Pediatrics)
Stanford University
“ Developing Gene and RNAi Based Therapies”
1100B CTRB
December 19, 2011
Stephen G. Kaler, M.D.
Head, Unit on Human Copper Metabolism, Molecular Medicine Program, NICHD
“ ATP7A Gene Therapy for Menkes Disease”
1100B CTRB



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